We’re thrilled to share that Alexander Rotenberg of the Kirby Neurobiology Center and Boston Children’s Hospital has been named a 2025 Harrington Scholar-Innovator by the Harrington Discovery Institute at University Hospitals!

Dr. Rotenberg’s project is titled “Gene therapy for a rare inherited disease, Succinic Semialdehyde Dehydrogenase Deficiency (SSADHD).”

SSADHD is a rare pediatric neurometabolic disorder with no approved treatments—and Dr. Rotenberg’s groundbreaking work is aiming to change that through targeted gene therapy.

This prestigious award supports physician-scientists advancing breakthrough treatments from bench to bedside. Dr. Rotenberg’s recognition is a powerful testament to his visionary science, relentless dedication, and commitment to families facing rare and often overlooked neurological diseases.

We’re incredibly proud to celebrate this honor with him and look forward to the impact his work will have on children and families around the world.